TOP TIERMARKET NEWSWIRE
Movers explained · 2026-09-03

Archived explainer. For the current picture see today's RARE page.

Why Is ULTRAGENYX PHARMACEU (RARE) Stock Down Today?

By the Top Tier Newswire AI Desk · September 3, 2026 at 9:31 AM ET · reviewed against 35 wire stories

ULTRAGENYX PHARMACEU (RARE) is down -47.08% in the latest session. Our newswire has captured 35 stories on RARE across 12 sources in the last 36 hours, with AI sentiment reading bearish (avg 32/100).

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Why RARE stock is down today

RARE stock is down 47.08% as of the latest trade at $14.04. The steep decline follows the announcement of a failed Phase 3 trial for Apazunersen in Angelman syndrome, which triggered a wave of price target cuts from analysts. The stock opened with a -45.4% gap down from the prior close, signaling immediate investor concern.

What Happened

Ultragenyx Pharmaceuticals reported that its Phase 3 ASPIRE trial for Apazunersen did not meet its primary or key secondary endpoints. This outcome led to a series of analyst actions, including Jefferies lowering its price target from $77 to $28, TD Cowen from $49 to $18, and Cantor Fitzgerald from $103 to $33. Wedbush also cut its target to $23 from $30. The drug trial failure has forced the company to reassess its strategy, with Barron's noting a focus on cost-cutting and the commercial business. Recent insider transactions show multiple sales by executives, including CFO Howard Horn and EVP Karah Herdman, totaling $417K in the last 90 days.

What The Data Shows

The stock opened at $14.48 and traded as low as $13.80, with volume reaching 3.1 million shares, 1.4 times the 3-month average. The market cap is $2.5 billion, with an unprofitable EPS TTM of -5.83 and a net margin of -81.7%. The stock has traded between $18.29 and $39.89 over the past 52 weeks. Over the last 8 sessions, the stock moved up slightly by 0.2% from $25.72 to $25.78. Social chatter has been minimal, with only one post in the last 24 hours and one in the last 7 days.

What To Watch

Investors should monitor the company's next steps in response to the trial failure. No earnings date is provided, but coverage breadth remains high with 35 stories from 12 sources in the last 36 hours. Analyst actions and any further updates on the drug program will be key.

AI-assisted analysis composed exclusively from headlines and data on the Top Tier newswire. Public view is delayed 4 hours from real time. Not financial advice.

RARE by the numbers

Last: $14.04Session: -47.08%7 sessions: -44.44%Coverage: 35 stories / 12 sourcesAI sentiment: 32/100 (bearish)Mkt cap: $2.5B52w: $18.29 to $39.89
RARE · Sep 3 session (5-min) · -43.78% vs prior close · updated 8:53 PM ET
$13.14$20.21$27.29prev close $26.53$14.917:00 AM10:13 AM1:27 PM4:41 PM7:55 PM7:00 AM · $14.567:05 AM · $14.247:10 AM · $14.207:15 AM · $14.367:20 AM · $14.307:25 AM · $14.157:30 AM · $14.177:35 AM · $14.137:40 AM · $14.337:45 AM · $14.127:50 AM · $14.227:55 AM · $14.088:00 AM · $13.948:05 AM · $13.908:10 AM · $13.908:15 AM · $14.258:20 AM · $14.168:25 AM · $14.108:30 AM · $14.058:35 AM · $14.058:40 AM · $14.088:45 AM · $13.988:50 AM · $13.908:55 AM · $13.959:00 AM · $14.059:05 AM · $14.209:10 AM · $14.179:15 AM · $14.109:20 AM · $14.159:25 AM · $14.009:30 AM · $14.029:35 AM · $14.179:40 AM · $14.629:45 AM · $14.579:50 AM · $14.919:55 AM · $14.8110:00 AM · $14.8710:05 AM · $14.7010:10 AM · $14.8310:15 AM · $14.7310:20 AM · $14.7210:25 AM · $14.7410:30 AM · $14.7010:35 AM · $14.7910:40 AM · $14.5410:45 AM · $14.5410:50 AM · $14.3310:55 AM · $14.3511:00 AM · $14.4811:05 AM · $14.3911:10 AM · $14.3711:15 AM · $14.3711:20 AM · $14.3811:25 AM · $14.4111:30 AM · $14.4411:35 AM · $14.5111:40 AM · $14.8111:45 AM · $14.8711:50 AM · $14.8711:55 AM · $14.8612:00 PM · $14.7512:05 PM · $14.8512:10 PM · $14.8812:15 PM · $14.9412:20 PM · $14.8512:25 PM · $14.9112:30 PM · $14.8912:35 PM · $14.9112:40 PM · $14.8512:45 PM · $14.7812:50 PM · $14.7912:55 PM · $14.781:00 PM · $14.771:05 PM · $14.671:10 PM · $14.531:15 PM · $14.571:20 PM · $14.621:25 PM · $14.601:30 PM · $14.541:35 PM · $14.541:40 PM · $14.551:45 PM · $14.541:50 PM · $14.611:55 PM · $14.602:00 PM · $14.682:05 PM · $14.702:10 PM · $14.722:15 PM · $14.762:20 PM · $14.722:25 PM · $14.622:30 PM · $14.602:35 PM · $14.712:40 PM · $14.702:45 PM · $14.712:50 PM · $14.692:55 PM · $14.743:00 PM · $14.723:05 PM · $14.683:10 PM · $14.603:15 PM · $14.673:20 PM · $14.733:25 PM · $14.803:30 PM · $14.813:35 PM · $14.783:40 PM · $14.833:45 PM · $14.853:50 PM · $14.853:55 PM · $14.844:00 PM · $14.804:05 PM · $14.794:10 PM · $14.904:15 PM · $14.874:20 PM · $14.874:25 PM · $14.934:30 PM · $14.904:35 PM · $14.864:40 PM · $14.844:45 PM · $14.854:50 PM · $14.834:55 PM · $14.835:00 PM · $14.865:05 PM · $14.825:10 PM · $14.815:15 PM · $14.845:20 PM · $14.845:25 PM · $14.845:35 PM · $14.845:40 PM · $14.835:45 PM · $14.815:50 PM · $14.845:55 PM · $14.836:00 PM · $14.826:05 PM · $14.836:10 PM · $14.816:15 PM · $14.826:20 PM · $14.826:25 PM · $14.836:30 PM · $14.886:35 PM · $14.896:40 PM · $14.856:45 PM · $14.866:50 PM · $14.896:55 PM · $14.887:00 PM · $14.887:05 PM · $14.897:10 PM · $14.887:15 PM · $14.897:20 PM · $14.857:25 PM · $14.887:30 PM · $14.897:35 PM · $14.947:40 PM · $14.947:50 PM · $14.927:55 PM · $14.91
AI sentiment, last 36h · averaged over 35 stories · 32/100 bearish
AI sentiment 32/100 (bearish)0 · bearish50bullish · 100

The headlines behind the move

Story flow · 8 stories on the wire, last 36h · hover or tap a dot for the headline
36h ago24h ago12h agopublishInvesting.com Analyst Ratings · sentiment 28 · Canaccord cuts Ultragenyx stock price target on trial failureInvesting.com Analyst Ratings · 28Canaccord cuts Ultragenyx stock price target on trial failureInvesting.com Analyst Ratings · sentiment 32 · H.C. Wainwright cuts Ultragenyx stock price target after trial missInvesting.com Analyst Ratings · 32H.C. Wainwright cuts Ultragenyx stock price target after trial missBarron's · sentiment 18 · Ultragenyx Stock Sinks 47% on Drug Trial Failure. Why Wall Street Isn’t Giving Up Yet.Barron's · 18Ultragenyx Stock Sinks 47% on Drug Trial Failure. Why Wall Street Isn’t Giving Up Yet.Bloomberg · sentiment 50 · US Stock Futures Today: Broadcom, HPE, Snowflake, UltragenyxBloomberg · 50US Stock Futures Today: Broadcom, HPE, Snowflake, UltragenyxThe Fly · sentiment 34 · Ultragenyx price target lowered to $23 from $30 at WedbushThe Fly · 34Ultragenyx price target lowered to $23 from $30 at WedbushThe Fly · sentiment 28 · Ultragenyx price target lowered to $33 from $103 at Cantor FitzgeraldThe Fly · 28Ultragenyx price target lowered to $33 from $103 at Cantor FitzgeraldThe Fly · sentiment 28 · Ultragenyx price target lowered to $18 from $49 at TD CowenThe Fly · 28Ultragenyx price target lowered to $18 from $49 at TD CowenThe Fly · sentiment 28 · Ultragenyx price target lowered to $28 from $77 at JefferiesThe Fly · 28Ultragenyx price target lowered to $28 from $77 at Jefferies
9d agoThe FlyBEARISH 28Analyst

Ultragenyx price target lowered to $28 from $77 at Jefferies

9d agoThe FlyBEARISH 28Analyst

Ultragenyx price target lowered to $18 from $49 at TD Cowen

10d agoThe FlyBEARISH 28Analyst

Ultragenyx price target lowered to $33 from $103 at Cantor Fitzgerald

10d agoThe FlyBEARISH 34Analyst

Ultragenyx price target lowered to $23 from $30 at Wedbush

10d agoBloombergNEUTRAL 50General

US Stock Futures Today: Broadcom, HPE, Snowflake, Ultragenyx

10d agoBarron'sBEARISH 18Earnings

Ultragenyx Stock Sinks 47% on Drug Trial Failure. Why Wall Street Isn’t Giving Up Yet.

Ultragenyx Pharmaceuticals looks to cut costs following the trial failure, while attention remains squared on its burgeoning commercial business.

10d agoInvesting.com Analyst RatingsBEARISH 32Analyst

H.C. Wainwright cuts Ultragenyx stock price target after trial miss

H.C. Wainwright cuts Ultragenyx stock price target after trial miss

10d agoInvesting.com Analyst RatingsBEARISH 28Analyst

Canaccord cuts Ultragenyx stock price target on trial failure

Canaccord cuts Ultragenyx stock price target on trial failure

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More on RARE: full news and sentiment history. Sentiment scores are AI-derived research signals, not financial advice.

Earlier RARE move explainers: 2026-09-04 · 2026-09-03